Empowering Patients 2025: A Cell and Gene Therapies Summit
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This free, virtual event in two half-day sessions offers educational discussions for foundation leaders, patients, and caregivers to better understand #GeneTherapy and #CellTherapy.
Hemophilia gene therapy webinar – December 4, 2024
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Scientific Advancements in Gene Therapies: Opportunities for Global Regulatory Convergence
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The Reagan-Udall Foundation for the FDA, in collaboration with the Bill & Melinda Gates Foundation, will host a hybrid public workshop on “Scientific Advancements in Gene Therapies: Opportunities for Global […]
State of the art of clinical stage gene therapies for Leukodystrophies – EURO NMD
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Educational webinars on rare neurological, neuromuscular and movement disorders jointly organized by the European Reference Networks for Rare Neurological Diseases (ERN-RND) and Neuromuscular Diseases (ERN-EuroNMD) and the European Academy of […]