Gene Therapy for IEI: It’s Taken Us So Long ‘Cause We’ve Got So Far To Come

Moderated by Dr. Jordan Orange, this important conversation will explore the progress, promise, and future of gene therapy for Inborn Errors of Immunity.
ISCT North America Regional Virtual Town Hall

Join ISCT on November 10 for an engaging Town Hall discussion on the real-world implementation of gene therapy for sickle cell disease (SCD). The session will be led by Dr. […]
Empowering Patients 2025: A Cell and Gene Therapies Summit

This free, virtual event in two half-day sessions offers educational discussions for foundation leaders, patients, and caregivers to better understand #GeneTherapy and #CellTherapy.
Hemophilia gene therapy webinar – December 4, 2024
Scientific Advancements in Gene Therapies: Opportunities for Global Regulatory Convergence

The Reagan-Udall Foundation for the FDA, in collaboration with the Bill & Melinda Gates Foundation, will host a hybrid public workshop on “Scientific Advancements in Gene Therapies: Opportunities for Global […]
State of the art of clinical stage gene therapies for Leukodystrophies – EURO NMD

Educational webinars on rare neurological, neuromuscular and movement disorders jointly organized by the European Reference Networks for Rare Neurological Diseases (ERN-RND) and Neuromuscular Diseases (ERN-EuroNMD) and the European Academy of […]